Clinical Trials Funded by the National Institute of Neurological Disorders and Stroke


  • A Phase I Study of Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Giant Axonal Neuropathy (website)
  • Exercise intervention for slowing HD progression (website)
  • Primary prevention of stroke in children with SCD in sub-saharan Africa II (website)
  • The effect of vitamin d3 on markers of oxidative stress in boys with x-linked ALD (website)
  • Tolerability of srx246 in Huntington’s disease patients (website)


  • A Phase II Trial of Rituximab In Myasthenia Gravis (website)


  • A Dose-Escalation, Safety And Feasibility Study Of Enteral Levetiracetam For Seizure Control In Pediatric Cerebral Malaria (website)
  • Duchenne Muscular Dystrophy: Double-blind Randomized Trial to Find Optimum Steroid Regimen (website)
  • Phase I/IIa Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA (website)
  • Phase 2 Clinical Trial of SGS-742 Therapy in Succinic Semialdehyde Dehydrogenase Deficiency (website)
  • Sickle Cell Disease – Stroke Prevention in Nigeria Trial (website)
  • Transcranial Magnetic Stimulation (TMS) in Spino-Cerebellar Ataxia (website)