National Center for Advancing Translational Sciences (NIH), USA


  • A targeted immunomodulator for the treatment of acute sickle crisis
  • Als clinical trials guidelines
  • Evaluation of a cathepsin s inhibitor as a potential drug for chagas disease
  • Evaluation of azd9291 in glioblastoma patients with activated egfr
  • Expansion of an efficient drug repurposing platform for rare genetic diseases
  • Fiber design and assessment for development of a novel biomimetic medical device
  • Rapid point-of-care diagnostic for early detection of dengue infection
  • Rapid, near-patient tests to monitor and guide therapy in sickle cell disease patients
  • Rare disease research training program
  • Wee1 and hdac inhibition in relapsed/refractory aml


  • Brittle bone disorders consortium of the rare disease clinical research network
  • Development of an ipsc-derived human vascular system for drug discovery and devel (website)
  • Fluorescent rna foci assay for fxtas drug discovery (website)
  • Phase i, sbir contract, n43tr-14-002?an assay to measure surrogate biomarkers for dmd?.


  • A new ctsa partnership to translate an oral cancer biomarker from lab to clinic (website)
  • Biocomputation across distributed private datasets to enhance drug discovery (website)
  • Comb External Beam Radiotherapy With 153sm-Edtmp To Treat High Risk Osteosarcoma
  • Development of a Biochemical Diagnosis for Creutzfeldt-Jakob disease (website)
  • Enzyme Replacement Therapy for Sanfilippo A Lysosomal Rare Disease (website)
  • Pancreatic Cancer: Assay for Early Detection (website)
  • Partnering to treat an Orphan Disease Duchenne Muscular Dystrophy (website)
  • Pharmacological Suppression of Rod Opsin as Therapy for Retinitis Pigmentosa (website)
  • Preclinical Development of Novel MEK1/2 Inhibitors to Treat Inherited Cardiomyopa (website)
  • Therapeutic Strategy for LAM (Lymphangioleiomyomatosis) (website)



  • A New CTSA Partnership to Translate an Oral Cancer Biomarker from Lab to Clinic (website)
  • Angelman Syndrome (AS) (website)
  • Assessing the Impact of Osteogenesis Imperfecta on Non-Skeletal Systems (website)
  • Early Detection of Pancreatic Cancer Using Ice COLD-PCR (website)
  • Modeling oxidative stress and DNA damage using GI organotypic culture systems (website)
  • Online patient self-assessment system for care and research of joint and skin dis (website)
  • Prader-Willi Syndrome (PWS) (website)
  • Wireless At-Risk Infant Monitoring System (website)



  • Drug Repurposing and Rediscovery for Gastrointestinal Stromal Tumors (website)