National Institutes of Health (NIH), USA

2013

  • 5-Hydroxymethylcytosine in Neurodevelopment (website)
  • A bifunctional nanomedicine for both specific imaging and targeting therapy of an (website)
  • A Drosophila Model for Charcot-Marie-Tooth 2B Disease (website)
  • A Drug Delivery Strategy for Targeted Therapy of Chronic Lymphocytic Leukemia (website)
  • A gene and prgenitor cell therapy in Huntington disease mice (website)
  • A Large Animal Model of SMA (website)
  • A Model System to Study Human Neuromuscular Disease (website)
  • A New Approach to ALS (website)
  • A new DMD model with a humanized glycome (website)
  • A Nonhuman Primate Model of Fragile X Associated Primary Ovarian Insufficiency (website)
  • A Novel Model of Medulloblastoma to Define Cancer Pathways and Molecular Targets (website)
  • A novel murine model for metastatic islet cell pancreas cancer (website)
  • A novel photopatterning-based paradigm for the study of 3D tumor infiltration (website)
  • A Predictive Prognostic Model for Glioblastoma Multiforme (website)
  • A role for elevated autophagy in survival and chemoresistance of leukemia stem ce (website)
  • A Surviorship Planning Tool for Head and Neck Cancer Patients and Caregivers (website)
  • AAV Mediated Gene Therapy to the CNS for MPS I (website)
  • Activity-Based Kinase Discovery In Small Cell Lung Cancer (website)
  • ADAM17 in pancreatic cancer and pancreatitis (website)
  • Add Health: A Genotype and Phenotype Resource for the Global Scientific Community (website)
  • Adoptive Immunotherapy for Multiple Myeloma Using Educated T Cells (website)
  • Adoptive Transfer of AlloCTL for Immunotherapy of Recurrent Gliomas (website)
  • Adult Neurological Phenotypes of Fragile X Gray Zone Expansion (website)
  • Advancing a Glioma Immunotherapy (website)
  • Aerobic glycolysis regulates apoptosis in neurogenesis and medulloblastoma (website)
  • Akt-EphA2 Crosstalk in Glioma Invasion (website)
  • Alpha M Beta 2 integrin blockade for acute inflammatory neuropathies (website)
  • ALS-associated TDP-43 Aggregation: A Drosophila Model and A Role for Autophagy (website)
  • Alterations in Blood-Brain/Blood-Spinal Cord Barrier Properties in Amyotrophic (website)
  • Alternative RNA splicing and protein products in leukemia outcome (PQ11) (website)
  • An Animal Model for Human Heart-Hand Syndromes (website)
  • An Animal Model of LRSAM1 Peripheral Neuropathy (website)
  • Analysis of autophagy and mitochondrial homeostasis in a human iPS model of NCL (website)
  • Analysis of LC-MS data to identify peptide and glycan biomarkers for hepatocellul (website)
  • Analysis of Risks and Outcomes for Rare Cancers (website)
  • Angiogenin in ALS Pathobiology and Therapy (website)
  • Animal models of autoimmune neuropathy (website)
  • Antibody-CpG conjugates for the treatment of B cell lymphoma (website)
  • Antisense oligonucleotide treatment for myotonic dystrophy (website)
  • Apical-basal polarity signaling in glioblastoma (website)
  • Ataxia gene identification by integrated genomic analysis (website)
  • Ataxin-2 as a genetic risk factor for ALS: New insights into neurodegeneration (website)
  • Autoimmune mechanisms in a novel Aire-deficient model of peripheral neuropathy (website)
  • Autophagic Clearance of Aberrant Tau: Biochemical and Therapeutic Implications (website)
  • Autophagy in Pancreatic Neuroendocrine Tumor Growth and Metastasis (website)
  • Axl as a target for the therapy of pancreatic cancer (website)
  • Axonal Transport Deficits during Hereditary Spastic Paraplegia (website)
  • Azithromycin to prevent BPD in ureaplasma-infected preterms (website)
  • B7-H1 expressing Macrophages Mediate Immunosupression in Glioma (website)
  • B7-H1 mediated immunosuppression in immunocompetent animal model of gliomas (website)
  • Balance and Posture in Adults with Cerebral Palsy (website)
  • Barriers to Early Detection of Esophageal Adenocarcinoma (website)
  • Baylor-Johns Hopkins Center for Mendelian Genetics (website)
  • BET bromodomain inhibition as targeted therapy in acute myeloid leukemia (website)
  • Biomarker Discovery for Early Detection of Pancreatic Ductal Adenocarcinoma (website)
  • Blocking TLR-Activation of Regulatory T cells Slows Disease in ALS (website)
  • Bone Marrow Microenvironment And Neuroblastoma Progression  (website)
  • Brain Cancer Stem Cell Reprogramming by c-Met (website)
  • Brain tumors with regulatory T-cells treated with EGFRvIII-specific T-cells (website)
  • Ca Signaling in Progression of Amyotrophic Lateral Sclerosis in Skeletal Muscle (website)
  • Calcium channels as novel therapeutic targets for Huntingtons Disease (website)
  • CD147 as a Novel Target in Head and Neck Cancer (website)
  • CD147 Biological Function and Role as a Biomarker of MGUS to Myeloma Progression (website)
  • CD38 Pretargeted Radioimmunotherapy for Myeloma (website)
  • CD44 Antagonists in Targeted and Combinational Therapy for Glioblastoma (website)
  • Cdk4/6 Inhibitor Therapy for Glioblastoma Multiforme (website)
  • CED of Nanoparticles Loading with Novel Agents for Improved Treatment of Gliomas (website)
  • Cell signaling as a leukemia biomarker (website)
  • Cell-Cell Transfer And Propagation Of Tau Aggregates (website)
  • Cellular and Genetic Basis of Anaplastic Medulloblastoma (website)
  • Cellular and Molecular Consequences of Respiratory Chain Defects in Neurons (website)
  • Cellular and Molecular Mechanisms of FUS-related Amyotrophic Lateral Sclerosis (website)
  • Cellular and Molecular Origins of Medulloblastoma Subgroups (website)
  • Cellular pathways underlying polyglutamine degeneration (website)
  • Cellular physiology of epilepsy-associated KCNQ2 channels (website)
  • Cellular plasticity and survival mechanisms in medulloblastoma stem cells (website)
  • Cellular Predisposition to Retinoblastoma Tumorigenesis (website)
  • Cerebellar Function in Health and Disease (website)
  • Cerebellar stimulation for the treatment of dystonia: preclinical studies (website)
  • Cerebral Malaria: Mechanisms of disease and neurological salvage (website)
  • Characterization of autonomic dysfunction in Rett syndrome & other MECP2 disorder (website)
  • Characterization of KIFAP3, a Modifier of Survival in Sporadic ALS (website)
  • Characterizing the Cells of Origin for Basal Cell Carcinoma (website)
  • Characterizing the glioma cell of origin in vivo using MADM, a mouse genetic mosa (website)
  • Characterizing the Role of NF-kB in Promoting Glioma Tumorigenicity (website)
  • Chemical Genetic Dissection of Aurora A in Promoting EMT and Stem Cells Phenotype (website)
  • Chemosensitization of Pancreatic Cancer Cells by Curcumin and Vitamin D Receptor (website)
  • Chronic Traumatic Encephalopathy: Clinical Presentation and Biomarkers (website)
  • Circulating Immune Biomarkers and Retinopathy of Prematurity (website)
  • Circumventing Barriers to Effective Oncolytic Virotherapy of Malignant Gliomas (website)
  • Clinical Implementation of Carrier Testing using NGS (website)
  • Clinical Therapy Trials (website)
  • Clinical Trial Planning in Pompe Disease (website)
  • Clinical Trials in Mesothelioma (website)
  • Clustering Postsynaptic Proteins at Neuromuscular Synapses: From Dok-7 to Rapsyn (website)
  • CNS mechanisms of developmental synapse elimination (website)
  • Cockayne syndrome: role of the innate immune response in neurodegeneration (website)
  • Cognitive Impairment Moderated by Working Memory in Pediatric Partial Epilepsy (website)
  • Collaborating Mutations in Medulloblastoma (website)
  • Comb External Beam Radiotherapy with 153Sm-EDTMP to Treat High Risk Osteosarcoma (website)
  • Combination therapy to inhibit neuroblastoma growth (website)
  • Combined Modality Targeted Therapy of Pancreatic Cancer with Death Receptor (website)
  • Companion Diagnostic for Multiple Myeloma (website)
  • Comparative Genomics Study of Foxa/ER Targets in Liver Cancer and Breast Cancer (website)
  • Completing genetic analysis of the ABCA4 locus (website)
  • Computerized Cognitive Rehabilitation in Children after Severe Malaria (website)
  • Conformational measurements of RyR1 using a site-specific labeling method (website)
  • Congenital brain malformations caused by aberrant head mesenchymal signaling (website)
  • Congenital Myasthenic Syndromes: Pathogenic Mechanisms (website)
  • Contribution of ASIC channels to intrinsic chemosensitivity of NTS neurons (website)
  • Crenolanib and ponatinib for the treatment of FLT3 mutant AML (website)
  • CRLF2 signaling in B-cell acute lymphoblastic leukemia (website)
  • Crosstalk between glioma cells &immune cells in the tumor microenvironment: Ther (website)
  • Cx26 mutations in syndromic deafness linked to skin disease (website)
  • Cytochrome C Oxidase in Malignant Gliomas (website)
  • Cytomegalovirus Gene Expression and Strain Variability in Glioma Pathogenesis (website)
  • Deciphering mechanisms of perivascular tumor cell invasion in glioblastoma (website)
  • Decisional Capacity and Informed Consent in Fragile X Syndrome (website)
  • Decoding the MST1 and MST2 kinases in cellular physiology and tumor suppression (website)
  • Defective c-MET signaling in African American scleroderma patients (website)
  • Defining mechanisms and targets in Wnt addicted human malignancies (PQ22) (website)
  • Defining PI3K p110alpha as a therapeutic target in pancreatic cancer (website)
  • Defining the metabolic phenotype of low grade gliomas in vivo (website)
  • Defining the role for Gle1 in the fetal lethal motor neuron disease LCCS1 (website)
  • Defining the role of mutant IDH in glioma initiation and maintenance (website)
  • Determinants of Neurodegenerative Decline in Primary Progressive Aphasia (website)
  • Developing a micorRNA-targeted therapy for ALS (website)
  • Developing diagnostic and therapeutic stem cells for cancer therapy (website)
  • Development and validation of prognostic model for gastric cancer (website)
  • Development of a HTS Assay for a Neurological Lysosomal Disease (website)
  • Development of a Porcine Model of Juvenile Neuronal Ceroid Lipofuscinosis (website)
  • Development of Clinical Strategies to Prevent GBM Recurrences After Radiotherapy (website)
  • Development of Inhibitors of the Leukemia Fusion Protein CBFbeta-SMMHC (website)
  • Development of New Therapeutics for Pancreatic Cancer Management (website)
  • Development of novel thiobarbituric acid analogs for malignant brain tumors (website)
  • Development of Oncolytic Adenovirus Targeting Pancreatic Cancer Stem Cells (website)
  • Development of sd-rxRNAs as Therapy for Retinoblastoma and Other Malignancies (website)
  • Development of TAK1 Inhibitors to Treat Pancreatic Cancer (website)
  • Dietary Selenium, Selenoenzyme Genes and Adult Glioma (website)
  • Differential Approach to the Postural Tachycardia Syndrome (website)
  • Diffuse Optical Monitoring of Head and Neck Tumor Therapy (website)
  • Discovering chemical tools for acute myelogenous leukemia (website)
  • Discovering More Juvenile Myoclonic Epilepsy Genes by a Consortium (website)
  • Discovery and Evaluation of Prioritized Mutations in Pancreatic Cancer (website)
  • Discovery and Optimization of AML Prognostic Biomarkers (website)
  • Discovery and Targeting of Apoptosis Resistance Mechanisms in High-Risk T-ALL (website)
  • Disease Mechanisms in Human Ubiquilinopathy (website)
  • Disruption of Cellular Messenger RNA Processing Events by the Kaposi’s Sarcoma-As (website)
  • Dissecting Hedgehog, TGF beta and BMP Signaling During Pancreatic Tumorigenesis (website)
  • Dissecting the genetic underpinnings of essential tremor (website)
  • Dissecting the mechanisms of immune tolerance within the pancreatic tumor’s micro (website)
  • Dissecting the role of cellular transport in neurodegeneration using A.nidulans (website)
  • DNMT3A Mutations In Acute Myeloid Leukemia (website)
  • Dopamine as a therapeutic agent in stomach cancer (website)
  • Dopamine D1 Receptor in mouse models of primary dystonia (website)
  • Drug Resistant Pathways in Relapsed Acute Lymphoblastic Leukemia(ALL) (website)
  • DUSP26: A Novel Therapeutic Target in Neuroblastoma (website)
  • DUX4 inhibition as a therapeutic strategy for FSHD (website)
  • Dysregulation of mTORC2 in gliomas (website)
  • Dystrophic Mouse Colony and Force Assessment (website)
  • Dystrophin Delivery To Muscle Via Myogenic Precursors  (website)
  • Early events of in vitro KSHV infection (website)
  • EFECAB: Improving pig management to prevent epilepsy in Burkina Faso (website)
  • Effect of early psychosine accumulation in Krabbe Disease on CNS progenitor cells (website)
  • Effect of high fat diet on pancreatic cancer in IKKa deficient mice (website)
  • Effect of NF1 mutation on choroid plexus function (website)
  • Effect of Omega-3 Fatty Acids on Cancer Stem Cells (website)
  • Effects of MH mutations on function of dihydropyridine receptor (website)
  • Effects of PolyQ Expansion on Full-length Huntingtin Protein in HD (website)
  • Effects of Strength Training on Bulbar Function in Amyotrophic Lateral Sclerosis (website)
  • Efficacy of flupirtine for treatment of neonatal hypoxic-ischemic encephalopathy (website)
  • Elucidating and understanding the genetic basis of movement disorders (website)
  • Elucidating mitochondrial pathomechanisms of ENT3 disorders in ENT3 KO mice (website)
  • Elucidating the Cellular and Molecular Mechanisms of Late-Onset Scoliosis (website)
  • Elucidating the Role of MiR-31 in Retinoblastoma Invasion (website)
  • Elucidating the role of TIN2L at the telomere and in dyskeratosis congenital (website)
  • Enabling use of blood spot cards for accurate high throughput Fragile X screening (website)
  • Endocytosis in JNCL (website)
  • Endoplasmic Reticulum Stress in Retinal Degeneration (website)
  • Energy Balance and Neurodegenerative Disease (website)
  • Engineering and Evaluation of Human L-Methionase for Cancer Therapy (website)
  • Enhancing the Biomedical Computing Platform for Pancreatic Cancer Research (website)
  • Enhancing Viral Oncolysis with Vasculostatin Gene Delivery (website)
  • Enzyme Replacement Therapy for Sanfilippo A Lysosomal Rare Disease (website)
  • Epi)Genomic drivers of primary and metastatic pancreatic islet cell carcinoma (website)
  • Epigenetic Markers in Huntington’s disease Brain (website)
  • Epigenetic Regulation of Heterochromatin Condensation in Huntington’s Disease (website)
  • Epigenomic Changes in Normal T-cell Development and Leukemogenesis (website)
  • Esophageal Adenocarcinoma Policy Model: Trends, Risk Factors and Screening (website)
  • Evaluating HMG-CoA reductase as a therapeutic target in ALS (website)
  • Evaluating the impact of KRas codon bias on pancreatic cancer (website)
  • Evaluation and treatment of enthesitis-related arthritis (website)
  • Evaluation of HCC Response to Systemic Therapy with Quantitative MRI (website)
  • Evaluation of MSP Antagonists for the Treatment of Pancreatic Cancer (website)
  • Evaluation of Patient-Matched Primary and Metastatic Samples to Identify and Vali (website)
  • Ewing’s Sarcoma Resistance to Immunity and Radiation (website)
  • EWS/FLI and its targets in Ewing’s sarcoma (website)
  • Exocytic pathways in HNSCC progression (website)
  • Exome sequencing in the skeletal dysplasias (website)
  • Experimental and Clinical Investigations of Retinal Stimulation (website)
  • Exploring Disease-Toxicant Interactions in a Human Huntington’s Disease Model (website)
  • Exploring Precision Cancer Medicine for Sarcoma and Rare Cancers (website)
  • Exploring the relationship of Vitamin D and childhood brain tumors (website)
  • Exploring the role of the de-ubiquitinase UCH-L1 in B-cell malignancy (website)
  • Expressive Language Sampling as an Outcome Measure (website)
  • ‘Exvading’Invasive Pediatric Brain Tumors (website)
  • Familial vertical talus exome sequencing (website)
  • Fate-mapping temporally marked precursor populations to hepatocellular carcinoma (website)
  • Flavonoids, esophageal/gastric cardia adenocarcinoma and Barretts Esophagus Risk (website)
  • Fragile X pre-mutation and ovarian insufficiency (website)
  • FSHD Bioresources Core (website)
  • FSHD iPS Cells: Genetic Correction and Myogenesis (website)
  • FSH-Patient Derived IPS Cells to Study the Developmental Regulation of DUX4 Trans (website)
  • Function and Regulation Mechanisms of Polo-like Kinase 3 in Pancreatic Cancer (website)
  • Function of the Zinc Finger Protein ZPR1 in neurodegeneration (website)
  • Functional characterization of astrocytes in a mouse model of Rett syndrome (website)
  • Functional Dissection of Huntington’s Disease Protein Huntingtin Using Drosophila (website)
  • Functional Evaluation of Human Pancreatic Cancer Genes in a Zebrafish System (website)
  • Functional Evaluation of microRNAs in Pancreatic Neoplasia (website)
  • Functional Genomics and Molecular Imaging of Liver Disease and Cancer (website)
  • Functional Imaging of Tremor Circuits and Mechanisms of Treatment Response (website)
  • Functional interactions among retinoschisin and its binding partners (website)
  • Functional Role of Micro RNAs in Huntington’s Disease Pathogenesis (website)
  • Functionizing the epigenome in Ewing sarcoma (website)
  • FUS/TLS gain And Loss Of Function In Als: Animal And Cellular Models Of Disease (website)
  • GABA System Alterations and Fragile X Syndrome (website)
  • Gene delivery for fukutin-related protein deficiencies (website)
  • Gene delivery to muscle and nerve for laminin-alpha2-deficient MD (MDC1A) (website)
  • Gene Discovery in Familial Keratoconus (website)
  • Gene Discovery in Muscular Dystrophy (website)
  • Gene discovery in primary dystonia using whole exome sequencing (website)
  • Gene discovery in PSP by transcriptome, neuropathology and sequence analysis (website)
  • Gene Therapy for Neurodegenerative Lysosomal Storage Diseases (website)
  • Gene therapy to support cone metabolism in retinitis pigmentosa (website)
  • Generation and Characterization of Novel Drosophila Models of TDP-43 Toxicity (website)
  • Genetic &immunologic etiology of chronic recurrent multifocal osteomyelitis-CRMO (website)
  • Genetic Basis of Syndromic and Non-Syndromic Congential Heart Defects (website)
  • Genetic Mechanisms for Conotruncal Heart Malformations (website)
  • Genetic Mechanisms of Non-syndromic Congenital Cardiac Defects (website)
  • Genetic network analysis of cancer targets (website)
  • Genetic Predictors of AML Treatment Response (website)
  • Genetic Risk Factors for Ewing’s Sarcoma (website)
  • Genetics and Genomics of Fuchs Endothelial Corneal Dystrophy (website)
  • Genetics of Familial Epilepsy Syndromes (website)
  • Genetics of Rhabdomyosarcoma (website)
  • Genome Studies in Hereditary Spastic Paraplegia (website)
  • Genome Wide Admixture Scan for Multiple Myeloma in African Americans (website)
  • Genome-wide Case-control Association Study of Pancreatic Cancer in Jews (website)
  • Genomic Diagnosis in Children with Developmental Delay (website)
  • Genomic Instability in Mouse Medulloblastoma (website)
  • Genomic Studies in Charcot-Marie-Tooth Disease (website)
  • Genotype and phenotype of chemoresistant AML (website)
  • Germline KLLN Alterations in PTEN Mutation Negative Cowden Syndrome (website)
  • Glaucoma Pathogenesis of Oculocerebrorenal syndrome of Lowe (website)
  • Gli Activity in the Pancreas:  Inflammation, Tissue Repair and Cancer (website)
  • Glioma immunotherapy with strategies based on autonomous parvovirus MVMp (website)
  • Graves’Disease Therapy Risks to Mother and Fetus (website)
  • Guanabenz in the treatment of mutant SOD1 ALS mice (website)
  • Guideline-based surveillance and treatment of hepatocellular carcinoma (website)
  • HDAC3 – a therapeutic target in PDA (website)
  • Head and Neck Cancer Risk Prediction Model (website)
  • Head and Neck squamous cell carcinoma radiation response modulation by HPV (website)
  • Hepatocyte Nox proteins in the pathogenesis of hepatocellular carcinoma (website)
  • HIF-2alpha mediated mitophagy and lipogenesis in clear cell renal cell carcinoma (website)
  • High Throughput Screening (HTS) to Discover Graft-Versus-Host Disease Inhibitors (website)
  • High Throughput Screening for Compounds to Mitigate Toxicity of FUS/TLS &SOD1 (website)
  • Human cytomegalovirus in the promotion of glioblastoma multiforme pathogenesis (website)
  • Human Minor Histocompatibity Antigens (website)
  • Hypersensitivity of Multiple Myeloma Bone Disease to Vitamin D (website)
  • Hypoxia-Selective Kinase Inhibitors for Leukemia Therapy (website)
  • Identification of genes causative for familial ALS gene using exome sequencing (website)
  • Identification of genes responsible for sarcolemmal integrity in C. elegans (website)
  • Identification of Immune modulators associated with JC virus replication (website)
  • Identification of mutation causing Purkinje cell degeneration in the shaker rat (website)
  • Identification of Novel X-linked Intellectual Disability Genes (website)
  • Identifying and Targeting Pathways of Pancreatic Cancer Progression (website)
  • Identifying Cell Stress Proteins that Predict Clinical Response in Pediatric AML (website)
  • Identifying Familial Pancreatic Cancer Predisposition Genes (website)
  • Identifying Regulators of Oncogenic CARD11 in Diffuse Large B Cell Lymphoma (website)
  • IDO-silencing Salmonella therapy for the treatment of primary and metastatic PDAC (website)
  • IGF1R gene 3′UTR variants in high-risk pediatric neuroblastoma (website)
  • Ikaros-based epigenetic regulation of T cell leukemogenesis (website)
  • IKKalpha, autophagy, obesity and injury enhanced pancreatic cancer (website)
  • Imaging Circuit Change in the Motor Cortex of Mouse Model of ALS (website)
  • Imaging Guided Genomics of Malignant Transformation (website)
  • Immortalized Human Strital Precursors as a Cell Model of HD (website)
  • Immunobiology and immunotherapy of pancreatic cancer (website)
  • Immunogene Therapy of Mesothelin Expressing Tumors Using Engineered T Cells (website)
  • Immunology Resource Core (website)
  • Immunotherapy against tauopathy in a transgenic mouse model (website)
  • Impact of B-Cell Lineage on Progression of B-Acute Lymphoblastic Leukemia (website)
  • Impact of molecular phenotype on glioma metabolism and growth (website)
  • Impact Of Motor Connectivity On Efficacy Of Hand Therapy In Congenital Hemiplegia (website)
  • Implications of a novel glioblastoma classification defined by miR-21-Sox2 status (website)
  • Improving Delivery of Molecularly-Targeted Therapy to Invasive Glioma Cells (website)
  • Improving Pancreas RT Plans using Respiration-driven Anatomic Deformation (website)
  • Improving T-cell therapies for neuroblastoma (website)
  • Improving therapy of glioblastoma multiforme by enhancing therapeutic drug delive (website)
  • In Vivo Function of Neuronal Activity-Induced MeCP2 phosphorylation (website)
  • In Vivo Lentiviral Gene Therapy for Hurler Syndrome (website)
  • In vivo magnetic resonance-based analysis of inherited neurologic disease after g (website)
  • Inactivation of Hdac3 in the cause, prevention, and treatment of HCC (website)
  • Inborn Errors of Metabolism Collaborative: Defining the Natural History of Inborn (website)
  • Indirubins: novel anti-invasive and anti-angiogenic drugs for malignant gliomas (website)
  • Infant and Toddler Brain Tumors (website)
  • Infectious origins of childhood leukemia (website)
  • Inflammasome function and SJIA (website)
  • Inhibiting glioma dispersal using non-toxic, natural products (website)
  • Inhibiting VHL-positive kidney cancer (website)
  • Inhibition of Autophagy Enhances Anti-Angiogenic Efficacy in Intracranial Glioma (website)
  • Innate and Adaptive Anti-Myeloma Immunity (website)
  • Innate immunity in Rett pathology and repair (website)
  • Innovative Efficacy Measures of Lupus Nephritis Therapies (website)
  • Integrative Genetic Analyses in Fuchs Endothelial Corneal Dystrophy (website)
  • Interferon Responses in Myeloid Leukemia (website)
  • International Case Control Study of Malignant Glioma (website)
  • Intracellular calcium leak and muscle function (website)
  • Intrathecal cyclodextrin therapy of feline Niemann-Pick type C disease (website)
  • Intra-tumoral Heterogeneity in Osteosarcoma: Tumorigenicity &Malignant Revision (website)
  • Invadopodia assembly in pancreatic tumor-associated fibroblasts (website)
  • Investigating a Toxic Gain-of-Interaction Between FUS/TLS &Stress Granules (website)
  • Investigating the pathogenesis of CoQ10 deficiencies (website)
  • Investigating the Role of Autophagy in Pancreatic Cancer Radiation Resistance (website)
  • Investigation of post-translational modifications in WT SOD1 in sporadic ALS (website)
  • Investigation Of Protocadherin-10 In Mef2- And Fmrp-Mediated Synapse Elimination (website)
  • In-vitro brain organotypic model of Progressive Multifocal Leukoencephalopathy (website)
  • IR signaling through PP6, a potential molecular target for radiosensitization (website)
  • Iron in the pathogenesis of Friedreich’s ataxia (website)
  • Isoform-specific effects of MeCP2 isoforms on neuronal viability (website)
  • Ki-Ras Signaling in Pancreatic Cancer: Role of a Novel Akt Regulator (website)
  • Knock-in Mice with Spinocerebellar Ataxia Type 13 Mutations in Kcnc3 (Kv3.3) Gene (website)
  • Linking Brain and Behavior in Chronic Tic Disorder (website)
  • Lipogenic inhibitors in prevention of oncogene induced liver cancer (website)
  • Liposome-siRNA-Peptide Complexes as Therapy to Cure Prion Diseases in Mouse Model (website)
  • LncRNA Pathways as Novel Diagnostic Biomarkers Derived from the Stroma of Epithel (website)
  • LRH-1: Structure-based Approach to Drug Design for Gastrointestinal Tumors (website)
  • LSDs:A Pilot NBS and Examination of the Associated Ethical Legal &Social Issues (website)
  • LuIII parvovirus targets glioma (website)
  • Lysophospholipids in Radiation Induced Signal Transduction in Malignant Gliomas (website)
  • Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy (website)
  • Magnetic-vortex microdiscs for glioma therapy (website)
  • Massively Parallel Sequencing for Familial Colon Cancer Genes (website)
  • Measles Virotherapy for Multiple Myeloma (website)
  • Mechanism of Merlin-mediated contact inhibition and tumor suppression (website)
  • Mechanism of Small Molecule Mediated Rescue of Mytonic Dystrophy (website)
  • Mechanism of SPARC peptide FSEC inhibition of angiogenesis in neuroblastoma (website)
  • Mechanism-Based Use of Chk1 Inhibitors in Pancreas Cancer (website)
  • Mechanisms and synergies of therapeutic drug treatments in muscular dystrophy (website)
  • Mechanisms of acquired temozolomide resistance in glioblastoma multiforme (website)
  • Mechanisms of degeneration in the spinal cord and musculoskeletal system in SMA (website)
  • Mechanisms of dysregulating MH RyR1s and their impact on bioenergetics (website)
  • Mechanisms of Embryonic Lens Determination (website)
  • Mechanisms of glioma growth and invasion novel therapeutic strategies (website)
  • Mechanisms of Krabbe Disease Pathobiology and Therapy (website)
  • Mechanisms of Metabolic Gene Mutations in Cancer (website)
  • Mechanisms of Mitochondrial Myopathy (website)
  • Mechanisms of Motor Skill Learning in the Fragile X Mouse Model (website)
  • Mechanisms of Neurodegeneration in ALS (website)
  • Mechanisms of Overexpressed TrkB in Inducing Pancreatic Cancer Metastasis (website)
  • Mechanisms of Pancreatic Tumor Nerve Invasion (website)
  • Mechanisms of PPM1D in medulloblastoma tumorigenesis and invasion (website)
  • Mechanisms of resistance to clinically-effective FLT3 kinase inhibitors in AML (website)
  • Mechanisms of T cell leukemia induction and maintenance (website)
  • Mechanisms of Transformation by TAL1/SCL in Thymic Malignancy (website)
  • Mechanisms of Valproic Acid-Induced Neurodevelopmental and Behavioral Defects (website)
  • Mechanisms Promoting Angiogenesis in Glioblastoma (website)
  • Mechanistic Dissection of the Fanconi Anemia Pathway of DNA Damage Response and R (website)
  • MeCP2 Modulation of BDNF Signaling: Shared Mechanisms of Rett and Autism (website)
  • MeCP2 regulation on LINE-1 retrotransposition in neurons (website)
  • Medulloblastoma and Metastases (website)
  • Merlin regulation of spinal cord NSC function (website)
  • Messenger RNA Stability in Myotonic Dystrophy (website)
  • Metabolic control of hepatocellular carcinoma by PGC1alpha (website)
  • Metabolic Regulators of Tumor Cell Growth (website)
  • Metabolic Reprogramming in Brain Tumors (website)
  • Metabolic Studies in Disorders of Branch Chain Amino Acid Metabolism (website)
  • Metabolite Profiling of a Novel Mitochondrial Kinase in Neuromuscular Disease (website)
  • Metachromatic Leukodystrophy Enzyme Drug Development (website)
  • Microbiomes in Human Pancreatic Cancer (website)
  • Microenvironmental impact on HNSCC response to targeted therapy (website)
  • Microparticles, a new player in cerebral malaria pathogenesis (website)
  • MicroRNA in Acute Myeloid Leukemia (website)
  • Microvesicles as potential genetic biomarkers of brain tumors (website)
  • Mining B-catenin/BCL9 transcriptional complex for Multiple Myeloma therapeutics (website)
  • Misregulation of the TDP-43 RNA target, Sortilin, in neurodegeneration (website)
  • Mitochondrial Gene Therapy (website)
  • Mitochondrial Homeostasis in Metabolically Distinct Subsets of B-Cell Lymphoma (website)
  • Mitochondrial Porin in Bioenergetic Defects in Huntingtons Disease (website)
  • Mitochondrial RNA transport as a novel therapy (website)
  • Model of Human Disc Regeneration in the spectrum of Degenerative Disc Disease (website)
  • Modeling Gene Regulation Essential for Long-Term Plasticity (website)
  • Modeling Mutant Profilin 1 Toxicity and ALS in vivo (website)
  • Models to predict prognosis and benefit from adjuvant therapy in renal cell carci (website)
  • Modulating aggrephagy to modify Huntington’s disease (website)
  • Modulating the levels of a splicing factor to reveal the complexities of a splice (website)
  • Modulating tolerance in a spontaneous mouse model of autoimmune vitiligo (website)
  • Modulation Of Cellular Clearance To Treat Human Disease (website)
  • Modulation of lysosomal function for the treatment of neuronal ceroid lipofuscino (website)
  • Molecular and Cellular Characterization of Prognostic Immune Response in Childhoo (website)
  • Molecular and cellular characterization of SMN-mediated U7 snRNP assembly (website)
  • Molecular basis for skeletal muscle pathophysiology in Pompe’s disease (website)
  • Molecular Basis of Iron Imbalance in sCJD Brain and CSF (website)
  • Molecular basis of Scapuloperoneal SMA and Charcot-Marie-Tooth disease type 2C (website)
  • Molecular epidemiology/functional analysis of microRNAs in Non-Hodgkin’s lymphoma (website)
  • Molecular genetic studies of progranulin regulators in FTLD and ALS (website)
  • Molecular Genetics of Dominant Neovascular Inflammatory Vitreoretinopathy (website)
  • Molecular interactions and restoration strategies of PTEN and p53 in gliomas (website)
  • Molecular Mechanism of Orlistat Hydrolysis by FASN for Targeted Drug Discovery (website)
  • Molecular mechanisms of GBM radioresistance and strategies for radiosensitization (website)
  • Molecular Mechanisms of Human Retinal Disease (website)
  • Molecular Mechanisms of IDH1-mediated Gliomagenesis (website)
  • Molecular Mechanisms of Primary Microcephaly (website)
  • Molecular Mediators of Pancreatic Cancer Invasion and Progression (website)
  • Molecular Pathogenesis and Treatment of MNGIE (website)
  • Molecular pathogenesis of MLL-AF4 leukemias (website)
  • Molecular Pathogenesis of Pediatric High-grade Glioma (website)
  • Molecular Pathways in T Cell Development and T-ALL (website)
  • Molecular Pathways Regulated By DUX4, an FSHD-Associated Gene (website)
  • Molecular Risk Assessment in Hereditary Melanoma (website)
  • Molecular Target Variation Across Environments and at Margins of Glioblastoma (website)
  • Molecular Targeting of Diffuse Large B-cell Lymphoma (website)
  • Molecular Targeting of L1CAM to Inhibit Glioblastoma Stem Cell Invasion (website)
  • Molecular Targeting Strategies in HNSCC (website)
  • Motion Management Using 4D-MRI for Liver Cancer in Radiation Therapy (website)
  • Motor Neuron Disease in Mouse Models of ALS: Where Does The End Begin (website)
  • Motor Planning in Children with Cerebral Palsy (website)
  • Mouse Models of Chronic Graft-vs-Host Disease (website)
  • Mouse Models of Human Conotruncal Defects (website)
  • Mouse Models to Define Critical Periods and Molecular Targets in FXTAS (website)
  • MR Imaging of IDH Mutational Status in Brain Tumors (website)
  • MR Investigation of IDH Mutation and Its Marker 2-HG in Brain Tumor Patients (website)
  • MRI Capable Receptor Targeted Drug Delivery for Pancreatic Cancer (website)
  • MRI of Iron-labeled Microsphere Biodistribution for Radioembolization Dosimetry (website)
  • MRI-based mapping of regional genomic diversity in Glioblastoma (website)
  • mtDNA heteroplasmy in development and differentiation: an in-vitro approach (website)
  • Multifunctional immunoPET tracers for pancreatic and prostate cancer (website)
  • Multifunctional nanoparticles to improve treatment of human glioblastoma (website)
  • Multipotential mesenchymal stem cell-like cells in pancreatic tumorigenesis (website)
  • Myb, a key driver of pancreatic cancer progression and metastasis (website)
  • Myxoma Virus (MV) Oncolysis for treating human cancer (website)
  • N-3 Fatty Acid-Induced Akt Suppression: Chemoprevention for Pancreatic Neoplasia (website)
  • Na-K-Cl cotransporter in Glioblastoma Multiforme (website)
  • Natural Killer Cell Based Immunotherapy  (website)
  • Naturally Occurring Dog Model for Juvenile Dermatomyositis (website)
  • NEK2 Over-expression Causes Drug Resistance in Myeloma (website)
  • Nested case-control study of maternal herpes viruses in relation to gastroschisis (website)
  • Neural mechanisms of texture processing in central and peripheral visual field (website)
  • Neurobiological Predictors of Huntington’s Disease (website)
  • Neurodegeneration and Proteotoxicity Dissected in C. elegans and Mammals (website)
  • Neurofibromin regulation of neural stem cell function in vitro and in vivo (website)
  • Neurogenesis: Career Development Plan in the Genetic and Modeling of Microcephaly (website)
  • Neuronal autophagy inducers as an approach to treat diseases of the central nervo (website)
  • Neuronal specific Autophagy Signaling (website)
  • New Insights into Motor Neuron Disease (website)
  • Next Generation gene discovery in neurogenetics (website)
  • Niemann-Pick C1: A New Compensatory Gene For Muscular Dystrophies  (website)
  • NMR Structural Studies of Ubiquitin Receptor Protein Complexes (website)
  • Noninvasive Assessment of Neuromuscular Disease using Electrical Impedance (website)
  • Non-Invasive Detection of Fetal Aneuploidy by Next-Generation DNA Sequencing (website)
  • Non-invasive Markers of Neurodegeneration in Movement Disorders (website)
  • Non-invasive sampling of DNA markers for pancreatic cancer screening (website)
  • Novel adhesion mechanisms in glioblastoma stem cells (website)
  • Novel Anti-HER3 Strategy for Pancreatic Cancer (website)
  • Novel Approaches to Graft-versus-Host Disease Prevention (website)
  • Novel Cell Cycle Therapeutic Targets in Pancreatic Cancer (website)
  • Novel Chemotherapeutics for Brain Tumors (website)
  • Novel Hedgehog Receptors As Therapeutic Targets In Pancreatic Cancer (website)
  • Novel high-throughput screening for modifiers of TorsinA pathology (website)
  • Novel lysine deacetylase 6 Hsp domain inhibitors against AML (website)
  • Novel mechanistic study of CMT2D neuropathy (website)
  • Novel monocyte effector function in CLL immune therapy (website)
  • Novel Nanoparticle Therapy for Pancreatic Cancer (website)
  • Novel Probes for Studying Treatment of CNS-based Lysosomal Storage Diseases (website)
  • Novel Targeted Therapy for AML (website)
  • Novel therapy for monoamine neurotransmitter deficiency in PKU (website)
  • Novel treatment strategies for enhancing sunitinib response in renal cell cancer (website)
  • Novel Vitamin B6 based prodrugs of gemcitabine (website)
  • Omega-3 Fatty Acids and Hepatic Carcinogenesis (website)
  • Optimization of compounds to improve mRNA splicing in familial dysautonomia (website)
  • Optimization of HDAC6 Inhibitors in the Treatment of CMT (website)
  • Optimization of Human iPS- Based Cell Therapy for Muscular Dystrophies (website)
  • Optimizing 131I-mIBG Therapy for Children with Advanced Neuroblastoma (website)
  • Optimizing selective in vivo inhibition of pancreatic tumor JAK2/STAT3 signaling (website)
  • Optogenetic control of striatal dopamine in Huntington’s disease (website)
  • Oral Biomarkers for HPV-related Head and Neck Cancer (website)
  • OSU-03012 therapy for glioblastoma (website)
  • Overcoming Evasion from Sorafenib in HCC (website)
  • Overcoming Immune Barriers to Gene Correction for Duchenne Muscular Dystrophy (website)
  • Overcoming Resistance to Anti-VEGF Treatment of Glioblastoma (website)
  • Overcoming Temozolomide Resistance using MGMT-targeting Spherical Nucleic Acids (website)
  • Overcoming therapeutic resistance of gliomas (website)
  • Oxysterol Biomarkers For Niemann-Pick C Disease (website)
  • P1 – Clinical Correlations of WTX Inactivation in Wilms Tumor (website)
  • p21-Activated Kinases as New Therapeutic Targets in Neurofibromatosis Type 1 (website)
  • P53-dependent GSTP1 Gene Regulation and Glioma Drug Resistance (website)
  • Partnering to treat an Orphan Disease Duchenne Muscular Dystrophy (website)
  • Pathogenesis and Therapy of Ichthyosis in Disorders of Lipid Metabolism (website)
  • Pathogenesis of Muscular Dystrophies (website)
  • Pathogenesis of Muscular Dystrophies (website)
  • Pathogenic impact of Huntington phosphorylation in Huntington’s Disease (website)
  • Pathogenic Mechanisms in Fragile X Tremor Ataxia Syndrome (website)
  • Pathogenic role of valosin-containing protein (VCP) in IBMPFD (website)
  • Pathway Specific Imaging in VHL Deficient Renal Cancer (website)
  • Peptide vaccine-based immunotherapy for children with recurrent ependymomas (website)
  • Peptide-targeted alpha-particle emitting phage for ovarian cancer therapy (website)
  • Peripheral blood biopsy for molecular diagnosis of pancreatic cancer (website)
  • Personal tumor neoantigens for immunity against chronic lymphocytic leukemia (website)
  • PGC-1alpha and GABAergic Dysfunction in Huntington Disease (website)
  • Ph 2 Study of Dextromethorphan in the Treatment of Rett Syndrome (website)
  • Ph 2 Study of Triheptanoin for Tx of Long-Chain Fatty Acid Oxidation Disorder (website)
  • Ph 2 Study of Vitamin D for Tx of Respiratory Complications in Sickle Cell Ds (website)
  • Ph2 of T-Cell Depl Familial Haploidentical SCT for tx Hi-Risk Sickle Cell Anemia (website)
  • Pharmacologic treatment of mitochondrial complex I dysfunction in C. elegans (website)
  • Pharmacological Suppression of Rod Opsin as Therapy for Retinitis Pigmentosa (website)
  • Phase 2 of  CellCept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis (website)
  • Phase 2 Study of Abatacept with Calcineurin Inhibition and Methotrexate for GVHD (website)
  • Phase 2 Study of ENB-0040 for the Treatment of Hypophosphatasia (website)
  • Phase 2 Study of Mexiletine for the Treatment of Myotonic Dystrophy (website)
  • Phase 2 Study of rhCC10 to Prevent Neonatal Bronchopulmonary Dysplasia (website)
  • Phase 2A Study of Exendin for the Treatment of Congenital Hyperinsulinism (website)
  • Phase 2B Trial of Memantine for the Treatment of Amyotrophic Lateral Sclerosis (website)
  • Phase II Trial of SGS-742 in Succinic Semialdehyde Dehydrogenase Deficiency (website)
  • Phosphoinositide Signaling Regulates Melanogenesis (website)
  • Phospho-valproic acid for pancreatic cancer prevention (website)
  • PhScN as a Potent Agent for Use with Radiation in Pancreatic Cancer (website)
  • Physiological mechanisms responsible for cognitive impairments in Dravet Syndrome (website)
  • Physiological significance of persistent inward currents in motor neurons (website)
  • Pilot newborn screening project for identification and prospective followup of in (website)
  • PKA and follicular thyroid carcinogenesis: Roles of interacting pathways (website)
  • PKCz;a novel therapeutic target for pancreatic cancer ‘stem cells’ (website)
  • Placode lineage contribution to Hirschsprung’s disease (website)
  • Polycomb and Cellular Hierarchy in the Brain (website)
  • Polysomy 21 in Acute Lymphoblastic Leukemia (website)
  • Pre-BCR and STAT5 Signaling in Acute Lymphoblastic Leukemia (website)
  • Preclinical Evaluation of ERBB Family Members as Therapeutic Targets in Osteosarc (website)
  • Preclinical Evaluation of Oncolytic HSV for Anaplastic Glioma Therapy (website)
  • Preclinical model of intra-arterial gene therapy for late infantile neuronal cero (website)
  • Preclinical Treatment for NF2-Associated Tumors (website)
  • Predicting toxicity and success of anti-GD2 immunotherapy of neuroblastoma (website)
  • Prediction of Pathologic Complete Response by Gene Expression Profiling in Esopha (website)
  • Predictors of myelodysplastic syndrome in Minnesota (website)
  • Presenilin dysfunction in the brain (website)
  • Pretherapy 124I-MIBG Dosimetry for Planning 131I-MIBG Neuroblastoma Therapy (website)
  • Preventing Glioma Cancer Stem Cell Dispersal Using Cdc2 Kinase Inhibitors (website)
  • Primordial germ cell differentiation and the initiation of testicular cancer (website)
  • Profiling Pancreatic Cancer Metabolism and Tumor Microenvironment for Therapy (website)
  • Prognostic and Functional Significance of Adhesion Molecules in Pediatric AML (website)
  • Progranulin interaction with Sortilin in FrontoTemporal Dementia (website)
  • Prospective Study of Clinically Non-functioning Pituitary Adenomas (website)
  • Prostaglandin E2 Signaling and Protection from Endoplasmic Reticulum Stress-Induc (website)
  • Protein and metal analysis core (website)
  • Protein Biomarkers in Childhood Acute Myeloid Leukemia (website)
  • Quantitative glycoproteomics for pancreatic cancer studies (website)
  • Quantitative MRI of Glioblastoma Response (website)
  • Quiescent Tc17 programmed CD8 T cells and their role in graft versus host disease (website)
  • rAAV-CNGB3 Gene Therapy for Achromatopsia: Translational Research Studies (website)
  • Racial Differences In Lung Adenocarcinoma Mutations (website)
  • Radiation Enhancement of HSV Anti-Tumor Effects (website)
  • Radioactive Stents for Brachytherapy of Esophageal Cancers (website)
  • Rare and Novel Genetic Variation in the Pathogenesis of Cerebellar Ataxia (website)
  • Rare Genetic Variants as Novel Causes of Idiopathic or Syndromic Short Stature (website)
  • Rare Protein Detection on Cell Surfaces: Ultrasensitive Detection of B-Cell Chron (website)
  • Real-time prediction of thermal ablation-induced cell death by echo decorrelation (website)
  • Redefining Langerhans Cell Histiocytosis as a Myeloid Dysplasia and Identifying B (website)
  • Reducing skeletal muscle fibrosis in DMD with AAV-delivered miR-29 (website)
  • Regenbase: A Searchable Database to Organize Regeneration Knowledge via Ontologie (website)
  • Regulation and function of Six1 in zebrafish muscle development and in rhabdomyos (website)
  • Regulation of Asymmetric Cellular Division in Glioma Stem Cells (website)
  • Regulation of caspase 9 RNA splicing in NSCLC cancer (website)
  • Regulation of Hypoxia-inducible Factor 1 by Cyclin Dependent Kinases (website)
  • Regulation of neural development by TGF beta family signaling (website)
  • Regulation of SMN and Identification of its Downstream Target (website)
  • Regulation of the Tumor Microenvironment in Hepatocellular Carcinoma (website)
  • Regulation, signaling, and dynamics of glucan phosphatases (website)
  • Response To Therapy For Patients With Glioma Using Hyperpolarized C-13 Pyruvate (website)
  • Restoring anti-tumor immunity in the microenvironment of head and neck cancer (website)
  • Retinal Iron Homeostasis in Health and Disease (website)
  • Revealing new regulators of EGFR-P13K driven glioma proliferation and migration (website)
  • Reversing BDNF Impairments in Rett Mice with TRPC Channel Activators (website)
  • RNA Regulation in FSHD (website)
  • RNA-Gain-of-Function Pathogenesis in SCA10 (website)
  • RNAi screen for chromatin regulators of differentiation in Acute Myeloid Leukemia (website)
  • RNAi screen of the glioblastoma stem cell kinome under hypoxia and normoxia (website)
  • RNAi therapy for Huntingtons disease: safety &efficacy in the nonhuman primate (website)
  • Role of a Novel Homeobox Transcription Factor (HLX) in Acute Myeloid Leukemia (website)
  • Role of ABC efflux transporters in ALS (website)
  • Role Of Aca11, An Orphan Small Nucleolar Rna In Resistance To Cancer Chemotherapy (website)
  • Role of Age in Liver Cancer (website)
  • Role of Ascl1 in glioma (website)
  • Role of ASK1 for GAPDH-Siah binding and GAPDH-Siah stress-signaling in HD (website)
  • Role of autoantibody isotype in pemphigus pathogenesis (website)
  • Role of Autotaxin in HCV-associated Hepatocellular Carcinoma (website)
  • Role of CCR2+ monocytes and Mo-DCs in defense against IA and GVHD development (website)
  • Role of cell cycle withdrawal in restricting pancreatic cancer progression (website)
  • Role of Cofilin and Wnt Signaling in Neural Crest Development (website)
  • Role of CTCF in Chromatin and Nuclear Organization at the FSHD 4qD4Z4Locus (website)
  • Role of C-type Lectin Receptors in Myeloid Plasticity in Neurocysticercosis (website)
  • Role of Dietary Zinc Transporter ZIP4 in Pancreatic Cancer (website)
  • Role of DNA Double Strand Break Response in Suppression of Thymic Lymphoma (website)
  • Role Of Dopamine Receptors In Primary Focal Dystonias (website)
  • Role of FUS in ALS (website)
  • Role of gammaherpesvirus lytic replication-associated genes in the establishment (website)
  • Role of genome organizer Satb1 in Shh-dependent proliferation and tumorigenesis (website)
  • Role of HSF1 in B cell activation and lymphoma (website)
  • Role of IDH1 and IDH2 Mutations in Glioma Cellular Biology and Pathogenesis (website)
  • Role of IRF4-NOTCH2 Interplay in B-Cell Development and Malignancy (website)
  • Role of MELK in glioblastomas (website)
  • Role of microRNAs in the regulation of CML stem cell survival and self renewal (website)
  • Role of MMP-9 in selective motor neuron degeneration in ALS (website)
  • Role of Neural Progenitor Cells in the Development of Neonatal Hydrocephalus (website)
  • Role of NKCC1 on Brain Tumor Stem Cell Migration After EGF and Slit-2 Stimulation (website)
  • Role of Obesity-Induced Immunosuppression in Pancreatic Cancer (website)
  • Role of Parkin in Familial and Idiopathic Parkinson’s Disease (website)
  • Role of Perinatal Neuronal Stem Cells in Tuber Formation (website)
  • Role of PLGF in Medulloblastoma Progression and Treatment (website)
  • Role of rac and reactive oxygen species in kaposi’s sarcoma viral  oncogenesis (website)
  • Role of Stasimon Dysfunction in Spinal Muscular Atrophy (website)
  • Role of TET2 mutations in malignant transformation and acute myeloid leukemia (website)
  • Role of the Giant Protein Titin in Skeletal Muscle Structure and Function (website)
  • Roles of Epstein-Barr virus nuclear antigens 2 and LP in B cell proliferation (website)
  • Roles of MiR-17-92 Cluster MicroRNAs in K-Ras-Induced Pancreatic Tumorigenesis (website)
  • Sclerostin Antibody Therapy for Treatment of Osteogenesis Imperfecta (website)
  • Screening for modulators of glioma stem cells differentiation (website)
  • Serum Glyco-Markers of Early Hepatocellular Carcinoma Using a Mass Spec Approach (website)
  • Serum IgE and Risk of Pancreatic Cancer (website)
  • SFRP2 and NFAT are therapeutic targets in angiosarcoma (website)
  • Sigma-2/Peptidomimetic Conjugates Target Apoptosis In Pancreatic Cancer (website)
  • Signaling Networks in Glioblastoma Drug Resistance (website)
  • Simultaneous attack of epithelial and stromal compartments in pancreatic cancer (website)
  • Skeletal Muscle Mechanisms of Disease in ALS (website)
  • Skin-targeted Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa (website)
  • Sleep and Circadian Rhythms in Tuberous Sclerosis Complex (website)
  • Sleeping Beauty Mediated Therapy for Alpha V Beta 6-Expressing Pancreatic Cancer (website)
  • Smith-Lemli-Opitz syndrome and Inborn Errors of Cholesterol Synthesis (website)
  • SMN Control of snRNP Biogenesis: Role in RNA Splicing and Motor Neuron Survival (website)
  • SPARC as a regulator of collagen signaling in Pancreatic Cancer (website)
  • Stat3 Signaling in Pancreas Cancer (website)
  • Stem cell mediated targeting of tumor cells and associated vasculature in gliomas (website)
  • Stem Cells, Differentiation and Therapeutic Resistance in AML (website)
  • Steroid Receptor Coactivator-2 as a key hepatic tumor suppressor and circadian me (website)
  • Strategies to Improve Kaposi’s Sarcoma Outcomes in Zimbabwe (website)
  • Strategies to overcome immunity in gene therapy of DMD (website)
  • Structure-Function Relationships in Dystonia: A Network Approach (website)
  • Studies of Childhood Sarcomas (website)
  • Study of Anti-Survival signals in NF1 (website)
  • Sunitinib Modulation of Cancer Immunotherapy (website)
  • Super-infection and virus spread during chronic hepadnaviral infection (website)
  • Suppression of BCR-ABL by siRNA-loaded Nanoparticles for the Treatment of CML (website)
  • Synaptic Contribution to Disease in Mouse Models of Charcot-Marie-Tooth (website)
  • Synaptic signaling in a human stem cell model of Angelman syndrome (website)
  • Synergistic interactions between SapC-DOPS and chemotherapy for glioma (website)
  • Synthesis of Vinblastine Analogues with Improved Physiochemical Properties (website)
  • Targeted Correction of Dominant Mutations of Type I Collagen Causing Severe OI (website)
  • Targeted Elimination of Cancer Stem Cells for AML Therapy (website)
  • Targeted Glycomics and Affinity Reagents for Cancer Biomarker Development (website)
  • Targeted Therapy for AML Stem Cells (website)
  • Targeted Therapy for Lymphoid Malignancies (website)
  • Targeting a non-canonical RAS-driven pathway in pancreatic cancer (website)
  • Targeting aberrant epigenetics by nanomedicine (website)
  • Targeting aml-stromal interactions (website)
  • Targeting Brain Tumor Stem Cells Through Novel Therapeutic Combinations (website)
  • Targeting fibrocytes in Duchenne muscular dystrophy (website)
  • Targeting glioma stem cells by perturbation of telomere maintenance mechanisms (website)
  • Targeting hypoxic microenvironment in Acute Lymphocytic Leukemia (website)
  • Targeting Membrane Repair in Muscular Dystrophy (website)
  • Targeting Mycn Protein With Small Molecules (website)
  • Targeting Myeloma Cell-Host Bone Marrow Interactions (website)
  • Targeting Negative Regulatory Pathways for Immunotherapy of B-Cell Lymphomas (website)
  • Targeting non-classical oncogenes as therapy for T-ALL (website)
  • Targeting Ovarian Tumor Associated Myeloid Cells with Nanoparticles Therapeutics (website)
  • Targeting Pancreatic Cancer Using Peptide Chemistry: From Bench to Bedside (website)
  • Targeting Pancreatic Cancer with Aptamers to the CCK-B Receptor (website)
  • Targeting proteostasis to treat Niemann-Pick C disease (website)
  • Targeting Radiation Resistance in Glioblastoma Stem Cells (website)
  • Targeting RAGE in pancreatic cancer (website)
  • Targeting Ras-Ral GEF-Ral Effector Signaling for Pancreatic Cancer Treatment (website)
  • Targeting SMN2 Alternative Splicing for the Treatment of Spinal Muscular Atrophy (website)
  • Targeting Stroma to Improve Therapy of Pancreatic Adenocarcinoma (website)
  • Targeting Stromal Collagen in Pancreatic Cancer (website)
  • Targeting SYK Tyrosine Kinase to Overcome Radiation Resistance in ALL (website)
  • Targeting Tau Splicing for Dementia (website)
  • Targeting the aberrant kinome-epigenome in AML (website)
  • Targeting the heat shock response for the therapy of DLBCL (website)
  • Targeting the Hedgehog Pathway in Pediatric Brain Tumors (website)
  • Targeting the JAK/STAT-3 Pathway Signaling Axis in Glioma (website)
  • Targeting the Lrp5 Pathway To Increase Bone Strength In Osteogenesis Imperfecta (website)
  • Targeting the MLL-WDR5 protein-protein interaction (website)
  • Targeting the PI3K/Akt pathway in High Grade Glioma (website)
  • Targeting the translational apparatus in MYCN-driven pediatric solid tumors (website)
  • Targeting the tumor matrix as anti-invasive and sensitizing strategy for glioma (website)
  • Targeting the Tumor Matrix as Anti-Invasive and Sensitizing Strategy for Glioma (website)
  • Targeting the Urokinase Receptor in Glioblastoma Multiforme (website)
  • Targeting to Epigenetic Modications in ALL (website)
  • Targeting vFLIP for the treatment of KSHV-associated malignancies (website)
  • T-cell Therapy for B-lineage Acute Lymphoblastic Leukemia (website)
  • Testing Direct Effects of Soy Daidzein on Fragile X Phenotypes (website)
  • Tetracycline derivatives as SMN2 mRNA splicing modifiers for treatment of SMA (website)
  • Th1/Th17 Cell Differentiation in GVHD and GVL (website)
  • Th1/Th17 Macrophage Interactions in Cutaneous GVHD (website)
  • The Basic and Translational Implication of SIRT1 and DNMT1 in Cancer (website)
  • The Effect of Aflatoxin Regulation on Global Liver Cancer Risk (website)
  • The effects of the unfolded protein response on medulloblastoma (website)
  • The essential role of supporting cells in medulloblastoma tumorigenicity (website)
  • The Fibrosis-Lymphedema Continuum in Head and Neck Cancer (website)
  • The Function of EBV LMP1 CTAR3 in Sumoylation and Oncogenesis (website)
  • The Functional Role of RBM45 in Gene Expression and Neurodegeneration (website)
  • The Gateway Hypothesis: A new framework for unraveling diverse leukodystrophies (website)
  • The Genetic and Epigenetic Basis for FSHD (website)
  • The Genetic Regulation and Disease Function of the Frontotemporal Dementia Protei (website)
  • The Genetics Of Ocular Melanoma  (website)
  • The Hippo Signaling Pathway in Pancreatic Cancer (website)
  • The impact of post-translational modification on SOD1 aggregation in ALS (website)
  • The Implications of Dystrophin-Specific T cells for DMD gene Correction (website)
  • The interaction of Burkitt???s lymphoma cofactors EBV and Plasmodium (website)
  • The interaction of IDO and Tregs Leads to Immunosuppression in Glioma (website)
  • The Mitochondrial Genome and Ovarian Cancer Risk (website)
  • The Molecular Function of D-cyclins in T-ALL (website)
  • The Nucleocytoskeleton in Progeria and Aging (website)
  • The Oncogenic Role of miR-9 in MLL-Associated Leukemias (website)
  • The Pathogenesis of Facioscapulohumeral Muscular Dystrophy (website)
  • The PPAR-delta pathway in neural function and Hungtington’s disease neuropatholog (website)
  • The role of a histone H4 phosphorylation in drug resistance (website)
  • The Role of Astrocytes in Huntington’s Disease (website)
  • The Role of Cul4A in Genome Stability and Cancer Development (website)
  • The Role of Desoxysphingoid Bases in HSAN1 (website)
  • The role of ETV6 in T-cell acute lymphoblastic leukemia (website)
  • The Role of Eya3 as a downstream target of EWS Fli1 in Ewings Sarcoma (website)
  • The Role of FBXL4 in T-cell Acute Lymphoblastic Leukemia (website)
  • The role of fractalkine signaling in neurodegenerative disease (website)
  • The Role of Growth Factor Receptor Trafficking in Tumorigenesis (website)
  • The Role of HMGB1 in the Pathogenesis of Mesothelioma (website)
  • The role of HO-1 in Flt3-ITD positive AML proliferation and drug resistance (website)
  • The Role of Huntingtin in Striatal Neurogenesis (website)
  • The role of ICSBP in the pathogenesis of chronic myeloid leukemia (website)
  • The Role of IL-17 Axis in Inflammatory Myositis (website)
  • The role of inhibitory receptors in leukemia development (website)
  • The Role of JAB1 in osteosarcoma pathogenesis (website)
  • The Role Of Lysophosphatidic Acid (LPA) And Its Receptor, LPA1 In Scleroderma (website)
  • The Role of Lysosomal Glucocerebrosidase in Synucleinopathies (website)
  • The role of microglial-and neuron-specific MyD88 signaling in tauopathies (website)
  • The role of microvesicles in giloma virotherapy (website)
  • The role of mir-17~92 cluster in motor neuron degeneration (website)
  • The role of miRNA15a and 16-1 in Multiple Myeloma (website)
  • The role of MTG8 in transcriptional elongation and leukemia (website)
  • The role of mTORC1 in the development and therapeutic targeting of NF1-associated (website)
  • The Role of NOTCH1 in the Pathogenesis of CLL (website)
  • The Role of p21-Activated Kinases in Malignant Mesothelioma (website)
  • The Role of RECQL4 in Bone Development and Osteosarcoma (website)
  • The role of RPTPzeta in models of Congenital Muscular Dystrophies (website)
  • The role of Sirt1 in Huntington’s Disease (website)
  • The role of spartin in autophagy of lipid droplets: Implications for SPG20 diseas (website)
  • The Role of Stroma-derived Soluble TbetaRIII in Neuroblastoma (website)
  • The Role of TDP-43 Phosphorylation in Protein Function and Neurodegeneration (website)
  • The Role of Telomere Shortening in MDS-AML Pathogenesis (resubmission) (website)
  • The Role of the APC Tumor Suppressor Gene in Hematopoiesis and Leukemogenesis (website)
  • The role of the stromal cell surface protease FAP in pancreatic cancer (website)
  • The Role of the Terminal Complement Pathway in ALS (website)
  • The Role of White Matter Progenitors in Glioma Formation and Progression (website)
  • The Roles of MicroRNAs in Glioblastoma (website)
  • The Roles of Tumor Microenvironment in Neurofibroma Development and Therapeutics (website)
  • The Tribbles-COP1 Complex in Leukemia (website)
  • Therapeutic Opportunities for Pediatric Astrocytoma (website)
  • Therapeutic Strategy for LAM (Lymphangioleiomyomatosis) (website)
  • Therapeutic Targeting of Leukemia-Microenvironmental Interactions (website)
  • Therapy for Spinal Muscular Atrophy (website)
  • Toll-like Receptor Regulation of Pancreatic Tumorigenesis (website)
  • TOR signaling and autophagy in obesity-promoted liver tumorigenesis (website)
  • TorsinA function and dystonia-related dysfunction in developing and mature CNS (website)
  • Toward understanding disease pathogenesis in the polyglutamine disorder Spinocere (website)
  • Tracking Neurodegeneration In Early Wolfram Syndrome (website)
  • Transcriptional regulation of gliomagenesis (website)
  • Transcriptome in Huntington’s disease and Huntington’s disease-like 2 (website)
  • Translating a CSF delivered AAV9-SMN for treatment of Spinal Muscular Atrophy (website)
  • Translating Novel Drug-Targetable Biomarkers to Treat Graft versus Host Disease (website)
  • Translation of Novel Therapeutic Targets in Multiple Myeloma (website)
  • Translation of smart contrast agents for brain tumor characterization by MR (website)
  • Translational Gene Therapy for Rhodopsin Autosomal Dominant Retinitis Pigmentosa (website)
  • Transponson-based screens for genes involved in acute lymphoblastic Leukemia (website)
  • Triptolide Augments Death Receptor Mediated Apoptosis in Pancreatic Cancer (website)
  • Tumor antigen-specific T-cells and hepatocellular carcinoma (website)
  • Tumor-produced TNF alpha as an inducer of immune resistance and tumor survival (website)
  • Understanding severe disruptive behaviors in adolescents with fragile X syndrome (website)
  • Understanding the Mechanisms of TDP-43 Function (website)
  • Understanding the role of MAPT in Parkinsonian disorders (website)
  • Understanding The Role Of Mitochondrial Import In Amyotrophic Lateral Sclerosis (website)
  • Unfolded Protein Response as a Therapeutic Target for ADRP Animal Models (website)
  • Using mouse models to understand retinoblastoma initiation and progression (website)
  • UW Center for Mendelian Genomics (website)
  • Validation of the HD-HRQOL (Huntington disease quality of life measure) (website)
  • Viral oncoprotein targeted immune therapy for Merkel cell carcinoma (website)
  • Virus nanoparticles as autophagy activators (website)
  • Vitamin D, cerebrovascular risk, and neurocognitive decline: ARIC Brain MRI Study (website)
  • Wild-type nerve grafting promotes reinnervation of SOD1 muscle (website)
  • Xenograft Model to Study Impact of CRLF2-Ligand in Hispanic Childhood B-ALL (website)
  • XIAP Gene Therapy in Huntington’s Disease (website)
  • Yale Center for Mendelian Genetics (website)
  • Zonule Assembly and Ectopia Lentis (website)